A baby born with a rare and life-threatening genetic disorder has taken his first steps after receiving a groundbreaking, personalized gene editing treatment at Children’s Hospital of Philadelphia. KJ ...
KJ Muldoon received a groundbreaking new treatment earlier this year. The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead ...
Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...
Every year, designers at Pew Research Center create hundreds of charts, maps and other data visualizations. We also help make a range of other digital products, from “scrollytelling” features to ...
A genetic disorder that leads to bleeding episodes and life-threatening infections has a new FDA approved treatment, a regulatory decision that marks two notable firsts — the first gene therapy for ...
The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the first therapy of its kind for the rare disease and making Italy’s Fondazione ...
Dec 9 (Reuters) - The U.S. Food and Drug Administration said on Tuesday it had approved the first gene therapy for a rare and life-threatening immune disorder. The therapy, Waskyra, was approved for ...
Kiss rocker Gene Simmons gives blunt advice to Dem senator’s son who dreams of having a music career
WASHINGTON — Kiss rocker Gene Simmons gave blunt advice on Tuesday to the music-loving son of Democratic Sen. Alex Padilla of California during a Senate hearing on legislation to pay recording artists ...
In a breakthrough study, scientists have discovered that a variant in one gene, GRIN2A, can directly cause mental illness – something previously believed to be the result of several mutations working ...
Scientists have identified a protein that may be key to proper sperm formation. Without it, male mice produced no viable sperm, they found. A team at the RIKEN Center for Biosystems Dynamics Research ...
Revolutions in gene therapy are rapidly changing the landscape of modern medicine. Revolutions in gene therapy are rapidly changing the landscape of modern medicine, forcing society and science alike ...
Nov 24 (Reuters) - (This Nov 24 story has been corrected to fix the pricing for Zolgensma to $2.5 million from $2.1 million in paragraph 4) The U.S. Food and Drug Administration has approved Novartis' ...
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